• 2013

Company Description

AveXis is a Biotech company is focused on developing gene therapy for patients with rare and life-threatening neurological genetic diseases.

Based in Dallas, Texas, AveXis is a clinic-ready, synthetic biology platform company. AveXis has, at its core, a desire to establish unique industry and research alliances which will bring innovative treatments to people with unmet medical needs. Our work in spinal muscular atrophy (SMA), a rare/orphan disease, is our first focus.